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Patient voice

How CLN2 Batten disease changed our life: “A Mother’s Love”

By Joe Rumney
16 May 2024

Industry Insights

What are the next steps for rare disease innovation in the United Kingdom?

By Joe Rumney
15 May 2024

RARE News

Global nonprofit CureDuchenne to host FUTURES National Conference for the Duchenne and Becker muscular dystrophy community (May 23-26, Orlando, Florida)

By Joe Rumney
14 May 2024

RARE News

Happy Heart Week: raising awareness of Barth syndrome—over a decade of hope and support

By Joe Rumney
9 May 2024
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