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World Orphan Drug Congress 15-18 November 2021 Melia Sitges Hotel Barcelona, Spain

Writing Orphan drug congress Europe - live and in person 15th-18th November 2021 Melia Sitiges Hotel Barcleona

The World Orphan Drug Congress is an award-winning event with an exhibition that has grown to become the largest and most established orphan drugs & rare diseases meeting of its kind across the globe. Now in its 12th annual edition, the World Orphan Drug Congress Europe, together with the co-located Cell & Gene Therapy Congress, will continue to bring experts from the whole value chain under one roof, where you get to meet decision makers in the areas that are most applicable for your business offering. 

2021 Congress Tracks:
 Cell & Gene Therapies       
 Genetic Testing
 Gene Editing
 Partnering & Investment
 Global Market Access
​ Expanded Access Programs 
 Real World Evidence

 Global Patient Advocacy
 Value Based Pricing & Reimbursement
 Epidemiology & Forecasting
 Orphan Drugs Policy
 Gene Therapy Development
 Clinical Trials
 Payers, HTA and Pricing
 Manufacture

Top Speakers include:
 Yann Le Cam, CEO, EURORDIS
 Frederic Revah,Chief Executive Officer, Genethon
 Anne Lee, Chief Pharmacist and Lead Officer, Scottish Medicines Consortium (SMC)
 Carla Deakin, Programme Director – Commercial & Managed Access, NICE
 Pierre Delsaux, Directorate-General for Health and Food Safety, European Commission
 Nathalie Moll, Director General, EFPIA
 Marcus Guardian,COO, EUnetHTA
 Sheela Upadhyaya, Accelerated Access Collaborative Relationship & Delivery Lead & HST, NICE
​ Giles Platford, COO, Takeda
 Daniel O’Connor, Expert Medical Assessor in Licensing Division,MHRA
 Daria Julkowska, Scientific Coordinator of the European Programme on Rare Diseases, INSERM
 Johanna Friedl-Naderer, President, Europe, Canada & Partner Markets, Biogen
 Vanessa Wolfeler, Global Franchise Head, Rare Blood Disorders, Sanofi Genzyme
 Paolo Martini, Chief Scientific Officer, Rare Diseases, Moderna Therapeutics
 Martin Dorazil, Deputy Head of Unit, European Reference Networks and Digital Health, DG SANTE, European Commission
 Francis Arickx, Head of the Directorate Reimbursement of Medicines and Pharmaceutical Policy, NIHDI – INAMI Belgium
​ Niklas Hedberg, Chief Pharmacist, TLV
 Wim Goettsch, Special Advisor HTA, ZIN 


Register below and use code RAREREV15 to receive 15% off your ticket.

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