Rare insights

Rare insights

CureDuchenne hosts conversation with Pfizer to discuss opening of first U.S. sites in phase 3 trial of investigational gene therapy for ambulatory patients with Duchenne muscular dystrophy

By admin

26 May 2022

Rare insights

The Vascular Birthmarks Foundation: revolutionising awareness levels, access to treatments and physician education

By CONTRIBUTOR

26 May 2022

Rare insights

Lace up to raise awareness of PSP and CBD: PSPA relaunches fun campaign to raise awareness of rare brain conditions progressive supranuclear palsy (PSP) and corticobasal degeneration (CBD)

By admin

23 May 2022

Rare insights

World Orphan Drug Alliance – combining forces to reach patients with rare diseases across the globe

By admin

23 May 2022

Rare insights

Rare Diseases Organization Nepal holds inaugural meeting to formalise its mission, vision, values and main objectives

By CONTRIBUTOR

23 May 2022

Rare insights

The World Orphan Drug Congress USA Boston July 11-13

By admin

23 May 2022

Rare insights

Saarah’s Foundation: a fitting legacy to Saarah Ahmed—daughter, sister, star student, aspiring neuroscientist, Miss Universe GB contestant and kEDS warrior

By CONTRIBUTOR

20 May 2022

Rare insights

Sure, you’ve heard about GNEM. But do you know about the Bulgarian variant?

By CONTRIBUTOR

19 May 2022

Rare insights

GARDIAN Registry for types 2 & 3 Gaucher disease is now open for registrations

By admin

17 May 2022

Rare insights

The first step in advocacy is believing in the power of your own voice

By CONTRIBUTOR

16 May 2022

Rare insights

Advocacy in Hemophilia Series: Event 1: Equity of Access in Hemophilia

By admin

12 May 2022

Rare insights

Conference to pave the way for the next decade of rare diseases

By admin

11 May 2022

Rare insights

Beat SCAD’s passionate and persistent quest for answers for the spontaneous coronary artery dissection community

By CONTRIBUTOR

9 May 2022

Rare insights

A story of heartbreak and hope: Juju’s journey with CLN2 Batten disease

By CONTRIBUTOR

9 May 2022

Rare insights

Building a bridge between patient and pharma: the CMT story

By CONTRIBUTOR

9 May 2022

Rare insights

The Big Sunflower Project

By CONTRIBUTOR

2 May 2022

Rare insights

National health charity CMTUK is to host annual conference on May 6th-7th

By admin

29 April 2022

« Previous 1 … 27 28 29 30 31 … 38 Next »