Rare insights

Rare insights

Launching CamRARE’s ‘The Need for a RARE Patient Passport’ Report for Rare Disease Day

By admin

1 March 2024

Rare insights

Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS

By admin

29 February 2024

Rare insights

SMA Europe launches “Care for adults living with SMA in Europe: a benchmarking report.”

By admin

29 February 2024

Rare insights

One in a million

By CONTRIBUTOR

28 February 2024

Rare insights

Raising a child with Hirschsprung’s disease

By CONTRIBUTOR

28 February 2024

Rare insights

300 million colours of Rare: three patients and caregivers share their rare disease stories

By CONTRIBUTOR

28 February 2024

Rare insights

Beyond development: Overcoming market access challenges for rare disease treatment

By CONTRIBUTOR

28 February 2024

Rare insights

£1.5 million new fund launched to ‘Help the Heart’

By admin

27 February 2024

Rare insights

Glasgow Children’s Hospital Charity: flying the flag for rare disease families year round

By CONTRIBUTOR

27 February 2024

Rare insights

CureDuchenne hosts “Champions in Miami” event on March 9 to help find a cure for Duchenne muscular dystrophy

By admin

23 February 2024

Rare insights

Guiding Grayson: a family’s fight to advocate, educate and save their son, Grayson, from CLN3 Batten Disease

By CONTRIBUTOR

21 February 2024

Rare insights

CMT Research Foundation partners to advance study of CMT type 1J by Dr Stephan Zuchner

By admin

21 February 2024

Rare insights

Dr Wendy Chung and Simons Searchlight: pioneering research into genes that cause rare neurodevelopmental disorders

By CONTRIBUTOR

21 February 2024

Rare insights

A day in the life: living with Bardet-Biedl syndrome—Tessa’s story

By CONTRIBUTOR

16 February 2024

Rare insights

Rare Disease Awareness Day Calendar

By CONTRIBUTOR

14 February 2024

Rare insights

Don’t let your condition define you! David’s journey with stiff person syndrome

By CONTRIBUTOR

14 February 2024

Rare insights

Rare Disease Day 2024: Sheela Upadhyaya previews some of the events taking place across the world

By CONTRIBUTOR

14 February 2024

« Previous 1 … 14 15 16 17 18 … 39 Next »