Rare insights

Rare insights

ARRE Foundation awards new research grant focused on ASXL3 disease mechanisms and future therapeutic development

By admin

22 May 2026

Rare insights

CureDuchenne appoints Lidia Gardner, PhD, EMBA, as vice president of clinical and medical affairs to advance patient-centered care, research, and strategic partnerships

By admin

22 May 2026

Rare insights

Fighting for life and hope

By CONTRIBUTOR

20 May 2026

Rare insights

The science of hope: a father’s race against the irreversible

By CONTRIBUTOR

13 May 2026

Rare insights

Listening to lead: how rare disease communities guide innovation

By CONTRIBUTOR

13 May 2026

Rare insights

Global nonprofit CureDuchenne to host FUTURES National Conference for the Duchenne and Becker muscular dystrophy community

By admin

5 May 2026

Rare insights

Navigating the future: iDR26, the 2026 International Drug Repurposing Conference

By admin

5 May 2026

Rare insights

From a moment, to momentum: Why Undiagnosed Day 2026 is shaping what happens next

By CONTRIBUTOR

29 April 2026

Rare insights

The power of your participation: strengthening data robustness and ethical trial design with natural history data

By CONTRIBUTOR

27 April 2026

Rare insights

Novartis receives EMA CHMP positive opinion for Itvisma, gene therapy for children two years and older, teens, and adults with spinal muscular atrophy (SMA)

By admin

24 April 2026

Rare insights

The student-led revolution in medical genetics

By CONTRIBUTOR

24 April 2026

Rare insights

Expediting novel therapies: a roadmap to a bright future for Saudi Arabia’s citizens

By Emma Bishop, RARE Revolution

22 April 2026

Rare insights

The invisible battle: how MSA rewrote my soul

By CONTRIBUTOR

19 April 2026

Rare insights

Rare but strong: turning a diagnosis into a community

By CONTRIBUTOR

18 April 2026

Rare insights

Research shows eye movement tests can help clinicians spot PSP earlier

By admin

17 April 2026

Rare insights

The diagnostic odyssey: how misdiagnosis and indication broadening can undermine rare disease clinical trials

By CONTRIBUTOR

8 April 2026

Rare insights

When strength looks like rest

By CONTRIBUTOR

8 April 2026

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