Rare insights

Rare insights

As we enter a new financial year, how does the UK Budget affect the rare disease community?

By CONTRIBUTOR

10 April 2024

Rare insights

Multidisciplinary expert panel explores the necessity to “shed light” on rare and undiagnosed diseases: an invitation to attend a live event at Harvard Medical School, in-person or virtually

By admin

10 April 2024

Rare insights

AKU Society launches Global Patient Registry to drive research into ultra-rare disease alkaptonuria

By admin

10 April 2024

Rare insights

New report: If Only You Knew

By admin

10 April 2024

Rare insights

Nxera Pharma joins the World Orphan Drug Alliance

By admin

9 April 2024

Rare insights

Eurordis to host 12th European Conference on Rare Diseases and Orphan Products (ECRD 2024)

By admin

4 April 2024

Rare insights

Miami community comes together for CureDuchenne, raising nearly $2.5M since 2021

By admin

3 April 2024

Rare insights

SMA Europe launches its 12th call for research

By admin

3 April 2024

Rare insights

Sickle Cell Disease Association of America promotes Kevin Amado Jr.

By admin

27 March 2024

Rare insights

How can we get the patient heard by the regulators?

By CONTRIBUTOR

27 March 2024

Rare insights

Eight challenges in developing rare disease therapies

By Nicola Miller, RARE Revolution

25 March 2024

Rare insights

Rare Disease Day 2024 – Call for greater awareness of X-linked adrenoleukodystrophy and cerebral adrenoleukodystrophy

By admin

20 March 2024

Rare insights

Rare disease advocates learn to accelerate therapeutic development at 9th RARE Drug Development Symposium

By admin

19 March 2024

Rare insights

Alnylam launches Hereditary ATTR (hATTR) Amyloidosis campaign to help shorten diagnosis time

By admin

19 March 2024

Rare insights

New primer highlights latest understanding of rare inherited disease alkaptonuria

By admin

19 March 2024

Rare insights

DEBRA UK asks the British public to BE the difference for EB in 2024

By admin

19 March 2024

Rare insights

Living well today: How do we make it happen for the rare diseases community?

By CONTRIBUTOR

13 March 2024

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